01:30:15

PPMD 2024 Annual Conference: Day 1 - Newly Diagnosed & Duchenne 101 Discussions

36:59

PPMD 2024 Annual Conference: Day 3 - OptimizeDMD: Moving the Dial in Endocrinology & Bone Issues

30:00

PPMD 2024 Annual Conference: Day 2 - KEYNOTE: Resilience

01:05:57

PPMD 2024 Annual Conference: Day 1 - Reporting to You on PPMD Professional Meetings

07:55

PPMD 2024 Annual Conference: Day 3 - Next Steps and Closing Remarks

55:59

PPMD 2024 Annual Conference: Day 2 - Decision Making around Steroids, Weight, and Nutrition

01:21:41

PPMD 2024 Annual Conference: Day 2 - Research Row: Strategies to Restore Dystrophin

21:30

PPMD 2024 Annual Conference: Day 3 - Your Citizen Science at Work: How Pain Impacts Quality of Life

48:44

PPMD 2024 Annual Conference: Day 3 - Clinical Trials: A Panel Discussion on the Developmental Path

47:37

PPMD 2024 Annual Conference: Day 3 - Research Row: PPMD Moving the Needle

38:06

PPMD 2024 Annual Conference: Day 3 - What really Matters: A Town Hall on Life, Living, and Hope

55:02

PPMD 2024 Annual Conference: Day 3 - Panel Conversation: Enhancing Social Experiences

39:21

PPMD 2024 Annual Conference: Day 1 - 30 Years Fighting for Every Future

41:45

PPMD 2024 Annual Conference: Day 1 - Outcome Measures: The Eras Tour

47:56

PPMD 2024 Annual Conference: Day 3 - Research Row: Approaches to Alter Progression

32:41

PPMD 2024 Annual Conference: Day 2 - KEYNOTE - A Reflection on Progress and Hope

47:28

PPMD 2024 Annual Conference: Day 3 - Panel Conversation: The Little Things Matter

43:27

PPMD 2024 Annual Conference: Day 2 - Current Approved Therapies Panel & Discussion (Pt. 2)

24:43

PPMD 2024 Annual Conference: Day 1 - Community Conversation With Pfizer

45:06

PPMD 2024 Annual Conference: Day 2 - How Managing Behaviors Impacts Your Quality of Life

01:53:29

PPMD 2024 Annual Conference: Day 1 - Navigating the Approved Therapy Landscape

27:49

PPMD 2024 Annual Conference: Day 1 - Building Your Community - It Takes a Team

57:45

PPMD 2024 Annual Conference: Day 2 - Sleep & Behavior: How They Impact Each Other

49:50

PPMD 2024 Annual Conference: Day 3 - Making Friends and ImPAACting People: A PAAC Presentation

58:10

Webinar: Community Progress in Duchenne Newborn Screening

01:01:30

Webinar: Community Update with ITF Therapeutics: Introducing DUVYZAT™ (givinostat) [March 2024]

45:03

Webinar: Sarepta Therapeutics - Data update from MOMENTUM study, SRP-5051 [Mar 2024]

39:33

Webinar: NS Pharma - Overview of New Exon Skipping Trials: Brogidirsen and NS-050/NCNP-03 (Mar 2024)

29:09

Webinar: PTC Therapeutics — EMFLAZA® Landscape in 2024

52:15

Webinar: Overview of WVE-N531 and the FORWARD-53 Clinical Trial with Wave Life Sciences [Feb 2024]

53:00

Webinar: Dyne Therapeutics — Advancing DYNE-251, an Investigational Medicine for DMD [Jan 2024]

01:00:58

Navigating Steroid Choices: Understanding the Process, Pathways, and Policies

13:27

Gene Therapy & Antibodies (Innovation Conversation with Barry Byrne, MD, PhD)

01:03:41

Webinar: Community Update on the New INSPIRE DUCHENNE Clinical Study of SGT-003

01:00:42

Webinar: AGAMREE® Approval with Catalyst Pharmaceuticals, Inc. [Nov 2023]

59:55

Webinar: Overview of Topline Results from Phase 3 EMBARK Study

50:51

AGAMREE Approval: What this means for you and your family

25:01

Advocating for Access: Overview of Medicaid DUR and P&T Meetings

54:28

Capricor Therapeutics: CAP-1002 HOPE-3 Program Update

49:31

Edgewise Therapeutics: A Novel Approach Designed to Protect Muscle in Becker Muscular Dystrophy

59:38

Supporting Families Through Decision Making

52:31

Webinar: Affinity Duchenne™ and Affinity Beyond™: Updates on Investigational RGX-202 from REGENXBIO

31:23

Advocating for Access: Insurance 101

07:21

Research Row Presentation: Viltepso (NS Pharma) - PPMD 2023 Annual Conference

29:12

Advocating for Access: Navigating Approved Therapies in Duchenne

04:03

ELEVIDYS and Genetic Variants

01:00:50

Research Row Breakout Session: PPMD Supported Research -- PPMD 2023 Annual Conference

59:37

Research Row Breakout Session: Approved or on the Horizon -- PPMD 2023 Annual Conference

16:26

Turning Adversity into Action: Your Power -- PPMD 2023 Annual Conference

54:57

Gene Therapy: The Power of Advocacy & Real World Evidence -- PPMD 2023 Annual Conference

11:49

Closing Remarks & Thank You -- PPMD 2023 Annual Conference

29:14

Ethics and Fair Play -- PPMD 2023 Annual Conference

52:15

Combination Therapies: How do We Get There? -- PPMD 2023 Annual Conference

01:05:25

Battling Behaviors -- PPMD 2023 Annual Conference

01:15:51

More than Puberty: The Impact of Testosterone -- PPMD 2023 Annual Conference

02:12:40

Gene Therapy Town Hall -- PPMD 2023 Annual Conference

01:26:09

Stronger With Every Beat -- PPMD 2023 Annual Conference

59:42

The Ins and Outs -- PPMD 2023 Annual Conference

01:09:39

Mental Wellness: Finding Balance -- PPMD 2023 Annual Conference

59:48

Research Row Breakout Session: Impacting Downstream -- PPMD 2023 Annual Conference